Brain transplantation of genetically corrected Sanfilippo type B neural stem cells induces partial cross-correction of the disease

Authors

Yewande Pearse, University of California, Los Angeles
Don Clarke, University of California, Los Angeles
Shih-Hsin Kan, University of California, Los Angeles
Steven Q Le, University of California, Los Angeles
Valentina Sanghez, University of California, Los Angeles
Anna Luzzi, University of California, Los Angeles
Ivy Pham, University of California, Los Angeles
Lina R Nih, University of California, Los Angeles
Jonathan D Cooper, Washington University School of Medicine in St. Louis
Patricia I Dickson, Washington University School of Medicine in St. Louis
Michelina Iacovino, University of California, Los Angeles

Journal

Molecular Therapy - Methods & Clinical Development

Publication Date

12-8-2022

Volume

27

First Page

452

Last Page

463

Document Type

Open Access Publication

DOI

10.1016/j.omtm.2022.10.013

Rights and Permissions

Pearse Y, Clarke D, Kan SH, Le SQ, Sanghez V, Luzzi A, Pham I, Nih LR, Cooper JD, Dickson PI, Iacovino M. Brain transplantation of genetically corrected Sanfilippo type B neural stem cells induces partial cross-correction of the disease. Mol Ther Methods Clin Dev. 2022 Oct 27;27:452-463. doi: 10.1016/j.omtm.2022.10.013. Copyright 2022 The Authors. This is an open access article under the CC BY-NC-ND license (http://creativecommons.org/licenses/by-nc-nd/4.0/).

Recommended Citation

Pearse, Yewande; Clarke, Don; Kan, Shih-Hsin; Le, Steven Q; Sanghez, Valentina; Luzzi, Anna; Pham, Ivy; Nih, Lina R; Cooper, Jonathan D; Dickson, Patricia I; and Iacovino, Michelina, "Brain transplantation of genetically corrected Sanfilippo type B neural stem cells induces partial cross-correction of the disease." Molecular Therapy - Methods & Clinical Development. 27, 452 - 463. (2022).
https://digitalcommons.wustl.edu/oa_4/1588

Department

ICTS (Institute of Clinical and Translational Sciences)

Additional Links

Supplemental material is available for this article at publisher site.