Journal
Neurology
Publication Date
1-28-2025
Volume
104
Issue
2
First Page
e210268
Document Type
Open Access Publication
DOI
10.1212/WNL.0000000000210268
Rights and Permissions
McMillan HJ, Baranello G, Farrar MA, Zaidman CM, Moreno T, De Waele L, Jong YJ, Laugel V, Quijano-Roy S, Mercuri E, Chien YH, Straub V, Darras BT, Seibert J, Bernardo Escudero R, Alecu I, Freischläger F, Muntoni F; SMART Study Group. Safety and Efficacy of IV Onasemnogene Abeparvovec for Pediatric Patients With Spinal Muscular Atrophy: The Phase 3b SMART Study. Neurology. 2025 Jan 28;104(2):e210268. doi: 10.1212/WNL.0000000000210268. This is an open access article distributed under the terms of the Creative Commons Attribution-Non Commercial-No Derivatives License 4.0 (CCBY-NC-ND), where it is permissible to download and share the work provided it is properly cited. The work cannot be changed in any way or used commercially without permission from the journal.
Recommended Citation
McMillan, Hugh J.; Zaidman, Craig M.; and et al., "Safety and efficacy of IV onasemnogene abeparvovec for pediatric patients with spinal muscular atrophy: The phase 3b SMART study." Neurology. 104, 2. e210268 (2025).
https://digitalcommons.wustl.edu/oa_4/5013
Department
ICTS (Institute of Clinical and Translational Sciences)
Additional Links
Supplemental material is available for this article at publisher site.
