A phase Ib/IIa clinical trial of dantrolene sodium in patients with Wolfram syndrome

Authors

Damien Abreu, Washington University School of Medicine in St. Louis
Stephen I. Stone, Washington University School of Medicine in St. Louis
Toni S. Pearson, Washington University School of Medicine in St. Louis
Robert C. Bucelli, Washington University School of Medicine in St. Louis
Ashley N. Simpson, Washington University School of Medicine in St. Louis
Stacy Hurst, Washington University School of Medicine in St. Louis
Cris M. Brown, Washington University School of Medicine in St. Louis
Kelly Kries, Washington University School of Medicine in St. Louis
Chinyere Onwumere, Washington University School of Medicine in St. Louis
Hongjie Gu, Washington University School of Medicine in St. Louis
James Hoekel, Washington University School of Medicine in St. Louis
Lawrence Tychsen, Washington University School of Medicine in St. Louis
Gregory P. Van Stavern, Washington University School of Medicine in St. Louis
Neil H. White, Washington University School of Medicine in St. Louis
Bess A. Marshall, Washington University School of Medicine in St. Louis
Tamara Hershey, Washington University School of Medicine in St. Louis
Fumihiko Urano, Washington University School of Medicine in St. Louis

Journal

JCI Insight

Publication Date

8-9-2021

Volume

6

Issue

15

First Page

e145188

Document Type

Open Access Publication

DOI

10.1172/jci.insight.145188

Rights and Permissions

Abreu D, Stone SI, Pearson TS, Bucelli RC, Simpson AN, Hurst S, Brown CM, Kries K, Onwumere C, Gu H, Hoekel J, Tychsen L, Van Stavern GP, White NH, Marshall BA, Hershey T, Urano F. A phase Ib/IIa clinical trial of dantrolene sodium in patients with Wolfram syndrome. JCI Insight. 2021 Aug 9;6(15):e145188. doi: 10.1172/jci.insight.145188. © 2021, Abreu et al. This is an open access article published under the terms of the Creative Commons Attribution 4.0 International License.

Recommended Citation

Abreu, Damien; Stone, Stephen I.; Pearson, Toni S.; Bucelli, Robert C.; Simpson, Ashley N.; Hurst, Stacy; Brown, Cris M.; Kries, Kelly; Onwumere, Chinyere; Gu, Hongjie; Hoekel, James; Tychsen, Lawrence; Van Stavern, Gregory P.; White, Neil H.; Marshall, Bess A.; Hershey, Tamara; and Urano, Fumihiko, "A phase Ib/IIa clinical trial of dantrolene sodium in patients with Wolfram syndrome." JCI Insight. 6, 15. e145188 (2021).
https://digitalcommons.wustl.edu/open_access_pubs/10817