Clinical trials for Wolfram syndrome neurodegeneration: Novel design, endpoints, and analysis models

Authors

Guoqiao Wang, Washington University School of Medicine in St. Louis
Zhaolong Adrian Li, Washington University School of Medicine in St. Louis
Ling Chen, Washington University School of Medicine in St. Louis
Heather Lugar, Washington University School of Medicine in St. Louis
Tamara Hershey, Washington University School of Medicine in St. Louis

Journal

PLoS One

Publication Date

1-1-2025

Volume

20

Issue

5

First Page

e0321598

Document Type

Open Access Publication

DOI

10.1371/journal.pone.0321598

Rights and Permissions

Wang G, Li ZA, Chen L, Lugar H, Hershey T (2025) Clinical trials for Wolfram syndrome neurodegeneration: Novel design, endpoints, and analysis models. PLoS One 20(5): e0321598. https://doi.org/10.1371/journal.pone.0321598. © 2025 Wang et al. This is an open access article distributed under the terms of the Creative Commons Attribution License, which permits unrestricted use, distribution, and reproduction in any medium, provided the original author and source are credited.

Recommended Citation

Wang, Guoqiao; Li, Zhaolong Adrian; Chen, Ling; Lugar, Heather; and Hershey, Tamara, "Clinical trials for Wolfram syndrome neurodegeneration: Novel design, endpoints, and analysis models." PLoS One. 20, 5. e0321598 (2025).
https://digitalcommons.wustl.edu/oa_4/5333

Department

ICTS (Institute of Clinical and Translational Sciences)

Additional Links

Supplemental material is available for this article at publisher site.