Journal
Journal of Clinical Investigation
Publication Date
12-1-2025
Volume
135
Issue
23
First Page
e182942
Document Type
Open Access Publication
DOI
10.1172/JCI182942
Rights and Permissions
Taghian T, Gallagher J, Bertrand S, Baker WC, Lopez Mercado K, Benatti HR, Hall E, Lopez Y, McElroy A, McCarthy JT, Pulaparthi S, Fernau D, Mather S, Esteves S, Diffie E, Gross A, Lahey HG, Jiang X, Parsley E, Gately R, Prestigiacomo R, Johnson S, Taylor A, Bierfeldt L, Tuominen S, Koehler J, Gao G, Xie J, Su Q, King R, Gounis MJ, Anagnostakou V, Puri A, Batista AR, Sena-Esteves M, Martin DR, Gray-Edwards H. Five-year analysis of efficacy and safety of a bidirectional AAV gene therapy in Tay-Sachs sheep. J Clin Invest. 2025 Sep 30;135(23):e182942. doi: 10.1172/JCI182942. : © 2025, Taghian et al. This is an open access article published under the terms of the Creative Commons Attribution 4.0 International License.
Recommended Citation
Taghian, Toloo; Jiang, Xuntian; and et al., "Five-year analysis of efficacy and safety of a bidirectional AAV gene therapy in Tay-Sachs sheep." Journal of Clinical Investigation. 135, 23. e182942 (2025).
https://digitalcommons.wustl.edu/oa_4/7689
Department
ICTS (Institute of Clinical and Translational Sciences)
Additional Links
Supplemental material is available for this article at publisher site.
