Preclinical studies in Krabbe disease: A model for the investigation of novel combination therapies for lysosomal storage diseases

Authors

Gregory Heller, University of Illinois at Chicago
Allison M Bradbury, The Ohio State University
Mark S Sands, Washington University School of Medicine in St. Louis
Ernesto R Bongarzone, University of Illinois at Chicago

Journal

Molecular Therapy

Publication Date

1-4-2023

Volume

31

Issue

1

First Page

7

Last Page

23

Document Type

Open Access Publication

DOI

10.1016/j.ymthe.2022.09.017

Rights and Permissions

Heller G, Bradbury AM, Sands MS, Bongarzone ER. Preclinical studies in Krabbe disease: A model for the investigation of novel combination therapies for lysosomal storage diseases. Mol Ther. 2023 Jan 4;31(1):7-23. doi: 10.1016/j.ymthe.2022.09.017. Copyright 2022 The Author(s). This is an open access article under the CC BY-NC-ND license (http://creativecommons.org/licenses/by-nc-nd/4.0/)

Recommended Citation

Heller, Gregory; Bradbury, Allison M; Sands, Mark S; and Bongarzone, Ernesto R, "Preclinical studies in Krabbe disease: A model for the investigation of novel combination therapies for lysosomal storage diseases." Molecular Therapy. 31, 1. 7 - 23. (2023).
https://digitalcommons.wustl.edu/oa_4/1649

Department

ICTS (Institute of Clinical and Translational Sciences)